| NCT06128629 |
PHASE3 |
RECRUITING |
Transthyretin Amyloidosis (ATTR) With Cardiomyopathy |
| NCT06672237 |
PHASE3 |
RECRUITING |
Neuromuscular Disease, Neuromuscular Diseases (NMD), Neurodegenerative Disease |
| NCT06634420 |
PHASE3 |
ACTIVE_NOT_RECRUITING |
Hereditary Angioedema |
| NCT06379789 |
PHASE1, PHASE2 |
RECRUITING |
Hemophilia B |
| NCT05120830 |
PHASE1, PHASE2 |
ACTIVE_NOT_RECRUITING |
Hereditary Angioedema |
| NCT06262399 |
— |
ENROLLING_BY_INVITATION |
Hereditary Angioedema |
| NCT05697861 |
— |
ENROLLING_BY_INVITATION |
Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy, Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy, Wild-Type Transthyretin Cardiac Amyloidosis |