Biotech Catalyst Calendar

32 upcoming clinical catalysts · sorted by expected readout

Upcoming readouts
BEAM2026-12BEAM2026-12CRSP2027-06CRSP2027-06VRTX2027-06VRTX2027-06NTLA2027-07VRTX2027-07

2026

ExpectedCompanyPhaseStatusIndication
2026-12 BEAM Recruiting Sickle Cell Trait
2026-12 BEAM PHASE1, PHASE2 Active Lymphoblastic Lymphoma, T-Cell Lymphoblastic Leukemia/Lymphoma, Lymphoblastic Leukemia

2027

ExpectedCompanyPhaseStatusIndication
2027-06 CRSP PHASE1 Recruiting Cardiovascular, Metabolic Disease, Dyslipidemias
2027-06-06 CRSP PHASE3 Active Sickle Cell Disease, Hydroxyurea Failure, Hydroxyurea Intolerance
2027-06-09 VRTX PHASE3 Recruiting Beta-Thalassemia, Thalassemia, Hematologic Diseases
2027-06-30 VRTX PHASE3 Recruiting Diabetes Mellitus, Type 1, Impaired Hypoglycemic Awareness, Severe Hypoglycemia
2027-07 NTLA PHASE3 Recruiting Neuromuscular Disease, Neuromuscular Diseases (NMD), Neurodegenerative Disease
2027-07-22 VRTX PHASE2 Recruiting Autosomal Dominant Polycystic Kidney Disease (ADPKD)
2027-09-30 VRTX PHASE3 Active Cystic Fibrosis
2027-11-14 CRSP PHASE3 Active Beta-Thalassemia, Thalassemia, Genetic Diseases, Inborn
2027-12 NTLA PHASE3 Recruiting Transthyretin Amyloidosis (ATTR) With Cardiomyopathy
2027-12-28 VRTX PHASE4 Enrolling Pain, Acute Postoperative, Breast Disease
2027-12-30 BEAM PHASE1, PHASE2 Recruiting Glycogen Storage Disease Type Ia

2028

ExpectedCompanyPhaseStatusIndication
2028-02 BEAM PHASE1, PHASE2 Active Sickle Cell Disease
2028-05 BEAM PHASE1, PHASE2 Recruiting Alpha 1-Antitrypsin Deficiency
2028-06-02 VRTX PHASE2, PHASE3 Recruiting Proteinuric Kidney Disease
2028-08 VRTX PHASE4 Upcoming Knee Arthritis, Knee Osteoarthritis
2028-12-29 VRTX PHASE2, PHASE3 Recruiting Primary Membranous Nephropathy

2029

ExpectedCompanyPhaseStatusIndication
2029-01-30 VRTX PHASE2 Enrolling Myotonic Dystrophy Type 1 (DM1)
2029-03-02 VRTX PHASE2 Recruiting Myasthenia Gravis, Generalized
2029-05-30 BEAM PHASE1 Recruiting T-Cell Acute Lymphoblastic Leukemia/Lymphoma
2029-07-30 VRTX PHASE3 Enrolling Cystic Fibrosis

2030

ExpectedCompanyPhaseStatusIndication
2030-01 CRSP PHASE1, PHASE2 Recruiting B-cell Lymphoma, Non-Hodgkin Lymphoma, B-cell Malignancy
2030-06-30 VRTX PHASE3 Active Cystic Fibrosis

2031

ExpectedCompanyPhaseStatusIndication
2031-12-31 CRSP PHASE1 Recruiting SLE (Systemic Lupus), Lupus Erythematosus, Systemic, Lupus Nephritis

2033

ExpectedCompanyPhaseStatusIndication
2033-12 CRSP PHASE1, PHASE2 Recruiting Warm Autoimmune Hemolytic Anemia (WAIHA), ITP - Immune Thrombocytopenia, Warm Autoimmune Hemolytic Anemia

2034

ExpectedCompanyPhaseStatusIndication
2034-08-14 NTLA PHASE1, PHASE2 Recruiting Hemophilia B

2038

ExpectedCompanyPhaseStatusIndication
2038-03 NTLA Recruiting Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy, Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy, Wild-Type Transthyretin Cardiac Amyloidosis
2038-08 CRSP Enrolling Hematologic Malignancy, Solid Malignancy

2039

ExpectedCompanyPhaseStatusIndication
2039-09-30 CRSP PHASE3 Enrolling Beta-Thalassemia, Thalassemia, Sickle Cell Disease

2040

ExpectedCompanyPhaseStatusIndication
2040-04 NTLA Enrolling Hereditary Angioedema

2043

ExpectedCompanyPhaseStatusIndication
2043-02-12 BEAM Recruiting Hemoglobinopathy, Sickle Cell Disease